In the last 10 years gene therapy has experienced a renascence thanks to the development of safer and more efficient gene transfer vectors and to the advances in the cell therapy field. This book brings together a comprehensive collection of gene therapy tools and their thera‐ peutic applications. The first part of the book covers different gene therapy vectors focusing on their advantages and disadvantages. The second part of the book gets into gene therapy applications, from the latest successes on clinical trials to the new gene therapy targets that are still under development. This book allows the reader.